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🌱 來自: Huppert’s Notes

Congenital Adrenal Hyperplasia🚧 施工中

Congenital Adrenal Hyperplasia

21-hydroxylase deficiency

•   Pathophysiology: Autosomal recessive genetic disorder. Most common congenital adrenal hyperplasia (90% cases). Depending on the severity of enzyme deficiency, there is classic CAH (which is further subdivided into virilizing or salt-wasting forms) and nonclassic CAH. Enzyme deficiency causes an inability to produce cortisol (and aldosterone in the salt-wasting forms), which leads to low cortisol, low or normal aldosterone, and high ACTH, and thus to increased adrenal stimulation which results in high DHEA.

-   Classic CAH

   More severe form

   Virilizing features: XX karyotype: Ambiguous genitalia, normal ovaries/uterus, XY karyotype: Precocious puberty

   Salt-wasting: Hypotension, hyperkalemia because of lack of aldosterone; emesis/dehydration in first 2–4 weeks of life

-   Nonclassic CAH

   More mild form

   Presents later in life with signs of androgen excess and without neonatal genital ambiguity; some patients are asymptomatic

•   Diagnosis: High levels of 17-OH progesterone, which is the normal substrate for 21-hydroxylase (test for stimulated levels)

•   Treatment: Administer steroids and mineralocorticoids, which turn off excess ACTH via a negative feedback loop. Can consider surgical correction of female genitalia, if abnormal.

17-hydroxylase deficiency

•   Clinical features: Hypertension, hypokalemia. XX karyotype: Phenotypic female, lack of secondary sexual development. XY karyotype: Complete male pseudohermaphorditism; characterized by external female genitalia with a blind-ending vagina but without a uterus or fallopian tubes.

•   Diagnosis: High aldosterone, low cortisol, low DHEA

11-hydroxylase deficiency

•   Clinical features: Hypertension, hypokalemia. XX karyotype: Labial fusion. XY karyotype: Precocious puberty.

•   Diagnosis: Low aldosterone, low cortisol, high DHEA